Publication:
Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1

dc.contributor.authorMistry, Pramod K. (57211953810)
dc.contributor.authorBalwani, Manisha (22133289200)
dc.contributor.authorBaris, Hagit N. (8608886300)
dc.contributor.authorTurkia, Hadhami Ben (6506812532)
dc.contributor.authorBurrow, T. Andrew (23394581000)
dc.contributor.authorCharrow, Joel (7004262624)
dc.contributor.authorCox, Gerald F. (7402494346)
dc.contributor.authorDanda, Sumita (23026963700)
dc.contributor.authorDragosky, Marta (6507896662)
dc.contributor.authorDrelichman, Guillermo (7801427001)
dc.contributor.authorEl-Beshlawy, Amal (6603278914)
dc.contributor.authorFraga, Cristina (57189444693)
dc.contributor.authorFreisens, Selena (57202019666)
dc.contributor.authorGaemers, Sebastiaan (57191345339)
dc.contributor.authorHadjiev, Evgueniy (57196470542)
dc.contributor.authorKishnani, Priya S. (55574227832)
dc.contributor.authorLukina, Elena (7006788246)
dc.contributor.authorMaison-Blanche, Pierre (55664875900)
dc.contributor.authorMartins, Ana Maria (55695498300)
dc.contributor.authorPastores, Gregory (7005660938)
dc.date.accessioned2025-07-02T12:14:31Z
dc.date.available2025-07-02T12:14:31Z
dc.date.issued2018
dc.description.abstract[No abstract available]
dc.identifier.urihttps://doi.org/10.1016/j.bcmd.2018.04.001
dc.identifier.urihttps://www.scopus.com/inward/record.uri?eid=2-s2.0-85046818875&doi=10.1016%2fj.bcmd.2018.04.001&partnerID=40&md5=f241923a9a655d1c3e862bb8a067ddc0
dc.identifier.urihttps://remedy.med.bg.ac.rs/handle/123456789/12927
dc.titleSafety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1
dspace.entity.typePublication

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